Kota Kinabalu: The US Food and Drug Administration (FDA) is currently considering the approval of the first gene therapy for Duchenne muscular dystrophy (DMD), bringing hope to patients with such condition.
Coalition Duchenne’s Founder, Catherine Jayasuriya ,who is a Sabahan living in California (USA), has been actively advocating for Malaysian patients to have access to these potential life-saving drugs once they become available.
She has collaborated with pharmaceutical companies and spoken at conferences to establish trial sites in Malaysia, aiming to ensure that patients can benefit from these advancements.