In conjunction with Rare Disease Day on 28 February, we reflect on the challenges faced by patients diagnosed with Spinal Muscul...

In conjunction with Rare Disease Day on 28 February, we reflect on the challenges faced by patients diagnosed with Spinal Muscular Atrophy (SMA), who continue to encounter significant clinical, financial, and systemic barriers in accessing treatment across Malaysia.

Our latest report, Advancing Equitable Access to Spinal Muscular Atrophy (SMA) Gene Therapy: Recommendations for Outcome-Based Financing and Sustainable Procurement, examines emerging gene therapies and explores the feasibility of an outcomes-based payment model (OBPM) within existing financing frameworks. It outlines practical steps to expand access while easing the burden on patients and caregivers.

The full report is now available on our website🗣️🗣️🗣️

At IDEAS, we remain committed to advancing research in this area to support more equitable and sustainable healthcare solutions.

#IDEASMalaysia